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1.
Current Strategies for Increasing Knock-In Efficiency in CRISPR/Cas9-Based Approaches.
Int J Mol Sci
; 25(5)2024 Feb 20.
Article
in English
| MEDLINE | ID: mdl-38473704
2.
The landscape of CRISPR/Cas9 for inborn errors of metabolism.
Mol Genet Metab
; 138(1): 106968, 2023 01.
Article
in English
| MEDLINE | ID: mdl-36525790
3.
Bone Growth Induction in Mucopolysaccharidosis IVA Mouse.
Int J Mol Sci
; 24(12)2023 Jun 08.
Article
in English
| MEDLINE | ID: mdl-37373036
4.
Mucopolysaccharidoses: Cellular Consequences of Glycosaminoglycans Accumulation and Potential Targets.
Int J Mol Sci
; 24(1)2022 Dec 28.
Article
in English
| MEDLINE | ID: mdl-36613919
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